{"id":4004,"date":"2018-04-25T00:03:37","date_gmt":"2018-04-25T00:03:37","guid":{"rendered":"https:\/\/www.progeriaresearch.org\/?page_id=4004"},"modified":"2023-09-21T12:15:37","modified_gmt":"2023-09-21T16:15:37","slug":"first-ever-demonstrate-survival-benefit-in-progeria","status":"publish","type":"page","link":"https:\/\/www.progeriaresearch.org\/bn\/first-ever-demonstrate-survival-benefit-in-progeria\/","title":{"rendered":"\u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u09ac\u09c7\u0981\u099a\u09c7 \u09a5\u09be\u0995\u09be\u09b0 \u09b8\u09c1\u09ac\u09bf\u09a7\u09be \u09aa\u09cd\u09b0\u09a6\u09b0\u09cd\u09b6\u09a8\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u09aa\u09cd\u09b0\u09a5\u09ae \u09a5\u09c7\u09b0\u09be\u09aa\u09bf"},"content":{"rendered":"<p>\u098f\u09aa\u09cd\u09b0\u09bf\u09b2 24, 2018: \u09a6\u09cd\u09af \u099c\u09be\u09b0\u09cd\u09a8\u09be\u09b2 \u0985\u09ab \u09a6\u09cd\u09af \u0986\u09ae\u09c7\u09b0\u09bf\u0995\u09be\u09a8 \u09ae\u09c7\u09a1\u09bf\u0995\u09c7\u09b2 \u0985\u09cd\u09af\u09be\u09b8\u09cb\u09b8\u09bf\u09af\u09bc\u09c7\u09b6\u09a8 (JAMA) \u098f \u09aa\u09cd\u09b0\u0995\u09be\u09b6\u09bf\u09a4 \u098f\u0995\u099f\u09bf \u09a8\u09a4\u09c1\u09a8 \u0997\u09ac\u09c7\u09b7\u09a3\u09be \u09b0\u09bf\u09aa\u09cb\u09b0\u09cd\u099f \u0995\u09b0\u09c7\u099b\u09c7 \u09af\u09c7 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac, \u098f\u0995\u099f\u09bf \u09ab\u09be\u09b0\u09cd\u09a8\u09c7\u09b8\u09be\u0987\u09b2\u099f\u09cd\u09b0\u09be\u09a8\u09cd\u09b8\u09ab\u09c7\u09b0\u09c7\u099c \u0987\u09a8\u09b9\u09bf\u09ac\u09bf\u099f\u09b0 (\u098f\u09ab\u099f\u09bf\u0986\u0987), \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u09ac\u09c7\u0981\u099a\u09c7 \u09a5\u09be\u0995\u09a4\u09c7 \u09b8\u09be\u09b9\u09be\u09af\u09cd\u09af \u0995\u09b0\u09c7\u099b\u09c7\u0964 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href=\"https:\/\/jamanetwork.com\/journals\/jama\/article-abstract\/2679278?redirect=true&amp;appId=scweb\" target=\"_blank\" rel=\"noopener noreferrer\"><b>\u0985\u09a7\u09cd\u09af\u09af\u09bc\u09a8\u09c7\u09b0 \u09ac\u09bf\u09ae\u09c2\u09b0\u09cd\u09a4 \u09aa\u09a1\u09bc\u09a4\u09c7 \u098f\u0996\u09be\u09a8\u09c7 \u0995\u09cd\u09b2\u09bf\u0995 \u0995\u09b0\u09c1\u09a8<\/b><\/a><\/p>\n<p><strong>\u09ae\u09bf\u09a1\u09bf\u09af\u09bc\u09be\u09b0 \u099c\u09a8\u09cd\u09af:\u00a0 <\/strong><\/p>\n<ul>\n<li><strong><a href=\"https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2018\/04\/PRF-JAMA-Announcement_Press-Release-1.pdf\">\u09aa\u09cd\u09b0\u09c7\u09b8 \u09b0\u09bf\u09b2\u09bf\u099c<\/a><\/strong><\/li>\n<li><strong><a href=\"https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2018\/04\/PRF-JAMA-Announcement-Infographic.pdf\">\u0987\u09a8\u09ab\u09cb\u0997\u09cd\u09b0\u09be\u09ab\u09bf\u0995<\/a><\/strong><strong>\u00a0<\/strong><\/li>\n<li><a href=\"https:\/\/www.dropbox.com\/sh\/uuq64xv0w0kfrcf\/AAACRWWU4ZKezFTksabaimzba?dl=0\" target=\"_blank\" rel=\"noopener noreferrer\"><strong>\u09ac\u09bf-\u09b0\u09cb\u09b2 \u09ad\u09bf\u09a1\u09bf\u0993<\/strong><\/a><\/li>\n<\/ul>\n<p><strong>\u098f\u09b0 \u09ab\u09b2\u09be\u09ab\u09b2\u00a0<\/strong><a href=\"https:\/\/www.progeriaresearch.org\/bn\/clinical-trials\/\"><strong>\u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u0995\u09cd\u09b2\u09bf\u09a8\u09bf\u0995\u09be\u09b2 \u09a1\u09cd\u09b0\u09be\u0997 \u099f\u09cd\u09b0\u09be\u09af\u09bc\u09be\u09b2<\/strong><\/a><strong>\u00a0Progeria \u09b8\u0999\u09cd\u0997\u09c7 \u0986\u099b\u09c7 \u098f\u09ac\u0982 \u098f\u099f\u09be \u0985\u09ab\u09bf\u09b8\u09bf\u09af\u09bc\u09be\u09b2!<\/strong>\u00a0 \u00a0\u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09cd\u09a8\u09bf\u09ac \u09ac\u09cd\u09af\u09ac\u09b9\u09be\u09b0 \u0995\u09b0\u09c7 \u0997\u09ac\u09c7\u09b7\u09a3\u09be, \u098f\u0995\u099f\u09bf \u09a7\u09b0\u09a8\u09c7\u09b0 \u09ab\u09be\u09b0\u09cd\u09a8\u09c7\u09b8\u09be\u0987\u09b2\u099f\u09cd\u09b0\u09be\u09a8\u09cd\u09b8\u09ab\u09c7\u09b0\u09c7\u099c \u0987\u09a8\u09b9\u09bf\u09ac\u09bf\u099f\u09b0 (\u098f\u09ab\u099f\u09bf\u0986\u0987) \u09af\u09be \u09ae\u09c2\u09b2\u09a4 \u0995\u09cd\u09af\u09be\u09a8\u09cd\u09b8\u09be\u09b0\u09c7\u09b0 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be\u09b0 \u099c\u09a8\u09cd\u09af \u09a4\u09c8\u09b0\u09bf \u0995\u09b0\u09be \u09b9\u09af\u09bc\u09c7\u099b\u09bf\u09b2, \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u0986\u09af\u09bc\u09c1 \u09ac\u09c3\u09a6\u09cd\u09a7\u09bf\u0995\u09c7 \u09b8\u09ae\u09b0\u09cd\u09a5\u09a8 \u0995\u09b0\u09c7\u0964 \u0995\u09cd\u09b2\u09bf\u09a8\u09bf\u0995\u09be\u09b2 \u099f\u09cd\u09b0\u09be\u09af\u09bc\u09be\u09b2\u09c7, \u09aa\u09cd\u09b0\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 27 \u099c\u09a8 \u09b6\u09bf\u09b6\u09c1 \u09ae\u09a8\u09cb\u09a5\u09c7\u09b0\u09be\u09aa\u09bf \u09b9\u09bf\u09b8\u09be\u09ac\u09c7 \u09a6\u09bf\u09a8\u09c7 \u09a6\u09c1\u09ac\u09be\u09b0 \u0993\u09b0\u09be\u09b2 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac \u0997\u09cd\u09b0\u09b9\u09a3 \u0995\u09b0\u09c7\u099b\u09bf\u09b2\u0964 \u098f\u0987 \u0997\u09ac\u09c7\u09b7\u09a3\u09be\u09b0 \u0995\u09a8\u09cd\u099f\u09cd\u09b0\u09cb\u09b2 \u09ac\u09be\u09b9\u09c1\u09a4\u09c7 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 \u09b6\u09bf\u09b6\u09c1\u09b0\u09be \u099a\u09bf\u0995\u09bf\u09ce\u09b8\u09be \u0995\u09b0\u09be \u09b0\u09cb\u0997\u09c0\u09a6\u09c7\u09b0 \u09ae\u09a4\u09cb \u098f\u0995\u0987 \u09ac\u09af\u09bc\u09b8, \u09b2\u09bf\u0999\u09cd\u0997 \u098f\u09ac\u0982 \u09ac\u09b8\u09ac\u09be\u09b8\u09c7\u09b0 \u09ae\u09b9\u09be\u09a6\u09c7\u09b6 \u09a8\u09bf\u09af\u09bc\u09c7 \u0997\u09a0\u09bf\u09a4, \u09af\u09be\u09b0\u09be \u0995\u09cd\u09b2\u09bf\u09a8\u09bf\u0995\u09be\u09b2 \u099f\u09cd\u09b0\u09be\u09af\u09bc\u09be\u09b2\u09c7\u09b0 \u0985\u0982\u09b6 \u099b\u09bf\u09b2 \u09a8\u09be \u098f\u09ac\u0982 \u09a4\u09be\u0987 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac \u0997\u09cd\u09b0\u09b9\u09a3 \u0995\u09b0\u09c7\u09a8\u09bf\u0964 \u09ab\u09b2\u09be\u09ab\u09b2\u0997\u09c1\u09b2\u09bf \u09aa\u09cd\u09b0\u09ae\u09be\u09a3 \u0995\u09b0\u09c7 \u09af\u09c7 \u09b6\u09c1\u09a7\u09c1\u09ae\u09be\u09a4\u09cd\u09b0 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be \u0995\u09cb\u09a8 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be\u09b0 \u09a4\u09c1\u09b2\u09a8\u09be\u09af\u09bc \u0989\u09b2\u09cd\u09b2\u09c7\u0996\u09af\u09cb\u0997\u09cd\u09af\u09ad\u09be\u09ac\u09c7 \u0995\u09ae \u09ae\u09c3\u09a4\u09cd\u09af\u09c1\u09b0 \u09b9\u09be\u09b0\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u09af\u09c1\u0995\u09cd\u09a4 \u099b\u09bf\u09b2 (3.7% \u09ac\u09a8\u09be\u09ae 33.3%) 2.2 \u09ac\u099b\u09b0\u09c7\u09b0 \u09ab\u09b2\u09cb\u0986\u09aa\u09c7\u09b0 \u09ae\u09be\u099d\u09be\u09ae\u09be\u099d\u09bf\u0964 \u0997\u09ac\u09c7\u09b7\u09a3\u09be\u09b0 \u09ab\u09b2\u09be\u09ab\u09b2 \u09af\u09be \u099b\u09bf\u09b2\u00a0<strong>\u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be \u09b0\u09bf\u09b8\u09be\u09b0\u09cd\u099a \u09ab\u09be\u0989\u09a8\u09cd\u09a1\u09c7\u09b6\u09a8 \u09a6\u09cd\u09ac\u09be\u09b0\u09be \u0985\u09b0\u09cd\u09a5\u09be\u09af\u09bc\u09a8 \u098f\u09ac\u0982 \u09b8\u09ae\u09a8\u09cd\u09ac\u09bf\u09a4<\/strong>, 24 \u098f\u09aa\u09cd\u09b0\u09bf\u09b2, 2018 \u09b8\u09be\u09b2\u09c7 \u09aa\u09cd\u09b0\u0995\u09be\u09b6\u09bf\u09a4 \u09b9\u09af\u09bc\u09c7\u099b\u09bf\u09b2 <em>\u0986\u09ae\u09c7\u09b0\u09bf\u0995\u09be\u09a8 \u09ae\u09c7\u09a1\u09bf\u0995\u09c7\u09b2 \u0985\u09cd\u09af\u09be\u09b8\u09cb\u09b8\u09bf\u09af\u09bc\u09c7\u09b6\u09a8\u09c7\u09b0 \u099c\u09be\u09b0\u09cd\u09a8\u09be\u09b2\u0964<\/em><\/p>\n<p><em>\u0997\u09b0\u09cd\u09a1\u09a8 \u098f\u099f\u0964 \u0986\u09b2\u0964, \u09b9\u09be\u099a\u09bf\u09a8\u09b8\u09a8-\u0997\u09bf\u09b2\u09ab\u09cb\u09b0\u09cd\u09a1 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be \u09b8\u09bf\u09a8\u09a1\u09cd\u09b0\u09cb\u09ae\u09c7 \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 \u09b0\u09cb\u0997\u09c0\u09a6\u09c7\u09b0 \u09ae\u09c3\u09a4\u09cd\u09af\u09c1\u09b0 \u09b9\u09be\u09b0\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be \u09ac\u09a8\u09be\u09ae \u0995\u09cb\u09a8\u0993 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be \u09a8\u09c7\u0987<\/em>, <em>JAMA, 24 \u098f\u09aa\u09cd\u09b0\u09bf\u09b2, 2018 \u09ad\u09b2\u09bf\u0989\u09ae 319, \u09b8\u0982\u0996\u09cd\u09af\u09be 16<\/em><strong>\u09ab\u09b2\u09be\u09ab\u09b2 \u09a8\u09a4\u09c1\u09a8 \u0986\u09b6\u09be \u098f\u09ac\u0982 \u0986\u09b6\u09be\u09ac\u09be\u09a6 \u09a8\u09bf\u09af\u09bc\u09c7 \u0986\u09b8\u09c7<br \/>\n<\/strong>\u09b6\u09bf\u09b6\u09c1\u09b0\u09be \u09ac\u09cd\u09af\u09be\u09aa\u0995 \u099a\u09bf\u0995\u09bf\u09ce\u09b8\u09be \u09aa\u09b0\u09c0\u0995\u09cd\u09b7\u09be \u098f\u09ac\u0982 \u0985\u09a7\u09cd\u09af\u09af\u09bc\u09a8 \u0993\u09b7\u09c1\u09a7 \u0997\u09cd\u09b0\u09b9\u09a3\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u09ac\u09cb\u09b8\u09cd\u099f\u09a8 \u099a\u09bf\u09b2\u09a1\u09cd\u09b0\u09c7\u09a8 \u09b9\u09be\u09b8\u09aa\u09be\u09a4\u09be\u09b2\u09c7 \u0997\u09bf\u09af\u09bc\u09c7\u099b\u09bf\u09b2\u0964 \u09b8\u09ac\u09be\u0987 \u09ae\u09cc\u0996\u09bf\u0995 \u09b2\u09cb\u09a8\u09be\u09ab\u09be\u09b0\u09a8\u09bf\u09ac 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\u09b8\u09b9-\u09aa\u09cd\u09b0\u09a4\u09bf\u09b7\u09cd\u09a0\u09be\u09a4\u09be \u098f\u09ac\u0982 \u09ae\u09c7\u09a1\u09bf\u0995\u09c7\u09b2 \u09a1\u09bf\u09b0\u09c7\u0995\u09cd\u099f\u09b0 \u098f\u09ac\u0982 \u09aa\u09cd\u09b0\u09a7\u09be\u09a8 \u0997\u09ac\u09c7\u09b7\u09a3\u09be \u09b2\u09c7\u0996\u0995 \u09ac\u09b2\u09c7\u099b\u09c7\u09a8\u0964<\/p>\n<p>\u201cPRF-\u098f, \u0986\u09ae\u09b0\u09be \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09b0 \u09b8\u09be\u09a5\u09c7 \u09ac\u09b8\u09ac\u09be\u09b8\u0995\u09be\u09b0\u09c0 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u09a8\u09a4\u09c1\u09a8 \u09ac\u09c8\u099c\u09cd\u099e\u09be\u09a8\u09bf\u0995 \u09b8\u09be\u09ab\u09b2\u09cd\u09af\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u0985\u09b0\u09cd\u09a5 \u099c\u09cb\u0997\u09be\u09a4\u09c7 \u0985\u0995\u09cd\u09b2\u09be\u09a8\u09cd\u09a4 \u09aa\u09b0\u09bf\u09b6\u09cd\u09b0\u09ae \u0995\u09b0\u099b\u09bf\u0964 \u098f\u0987 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\u0986\u09ae\u09b0\u09be \u0986\u0997\u09c7\u09b0 \u099a\u09c7\u09af\u09bc\u09c7 \u0986\u09b0\u0993 \u09b6\u0995\u09cd\u09a4\u09bf\u09b6\u09be\u09b2\u09c0 \u09ac\u09cb\u09a7 \u0985\u09a8\u09c1\u09ad\u09ac \u0995\u09b0\u09bf\u0964 \u0986\u099c\u0995\u09c7\u09b0 \u09ae\u09be\u0987\u09b2\u09ab\u09b2\u0995 \u098f\u0987 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u098f\u09ac\u0982 \u09a4\u09be\u09a6\u09c7\u09b0 \u09aa\u09b0\u09bf\u09ac\u09be\u09b0\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u098f\u0995\u099f\u09bf \u09a8\u09a4\u09c1\u09a8 \u09b8\u09c2\u099a\u09a8\u09be \u099a\u09bf\u09b9\u09cd\u09a8\u09bf\u09a4 \u0995\u09b0\u09c7\u09f7 \u09aa\u09cd\u09b0\u09a4\u09bf\u099f\u09bf \u09a6\u09bf\u09a8 \u098f\u09ac\u0982 \u09aa\u09cd\u09b0\u09a4\u09bf\u099f\u09bf \u09ae\u09c1\u09b9\u09c2\u09b0\u09cd\u09a4 \u0997\u09a3\u09a8\u09be\u0964 \u09aa\u09bf\u0986\u09b0\u098f\u09ab-\u098f\u09b0 \u09b2\u0995\u09cd\u09b7\u09cd\u09af \u09b9\u09b2 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09b0 \u09a8\u09bf\u09b0\u09be\u09ae\u09af\u09bc \u0996\u09c1\u0981\u099c\u09c7 \u09ac\u09c7\u09b0 \u0995\u09b0\u09be \u098f\u09ac\u0982 \u098f\u0987 \u0985\u09a7\u09cd\u09af\u09af\u09bc\u09a8\u099f\u09bf \u0986\u09ae\u09be\u09a6\u09c7\u09b0 \u09b8\u09c7\u0987 \u09b2\u0995\u09cd\u09b7\u09cd\u09af\u09c7\u09b0 \u09a6\u09bf\u0995\u09c7 \u0986\u09b0\u0993 \u098f\u0995\u099f\u09bf \u09aa\u09a6\u0995\u09cd\u09b7\u09c7\u09aa \u09a8\u09bf\u09af\u09bc\u09c7 \u0986\u09b8\u09c7, &quot;\u09aa\u09bf\u0986\u09b0\u098f\u09ab\u09c7\u09b0 \u09aa\u09cd\u09b0\u09c7\u09b8\u09bf\u09a1\u09c7\u09a8\u09cd\u099f \u098f\u09ac\u0982 \u09a8\u09bf\u09b0\u09cd\u09ac\u09be\u09b9\u09c0 \u09aa\u09b0\u09bf\u099a\u09be\u09b2\u0995 \u09ae\u09c7\u09b0\u09bf\u09b2 \u09ab\u09bf\u0999\u09cd\u0995 \u09ac\u09b2\u09c7\u099b\u09c7\u09a8<\/p>\n<p><strong>\u09ae\u09bf\u09a1\u09bf\u09af\u09bc\u09be \u0995\u09ad\u09be\u09b0\u09c7\u099c<\/strong><\/p>\n<p>\u098f\u0996\u09be\u09a8\u09c7 \u09aa\u09cd\u09b0\u09be\u09aa\u09cd\u09a4 \u09aa\u09cd\u09b0\u09c7\u09b8 \u0995\u09ad\u09be\u09b0\u09c7\u099c\u09c7\u09b0 \u098f\u0995\u099f\u09bf \u09a8\u09ae\u09c1\u09a8\u09be \u09b0\u09af\u09bc\u09c7\u099b\u09c7:<\/p>\n<ul>\n<li><strong>MedPage \u0986\u099c<br \/>\n<\/strong><a href=\"https:\/\/www.medpagetoday.com\/blogs\/themethodsman\/72505\" target=\"_blank\" rel=\"noopener noreferrer\"><em>\u09a1\u09cd\u09b0\u09be\u0997 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u0995\u09c7 \u09aa\u09b0\u09bf\u099a\u09be\u09b2\u09a8\u09be\u09af\u09cb\u0997\u09cd\u09af \u0995\u09b0\u09c7 \u09a4\u09c1\u09b2\u09a4\u09c7 \u09aa\u09be\u09b0\u09c7 <\/em><\/a><\/li>\n<li><strong>\u09ac\u09cb\u09b8\u09cd\u099f\u09a8 \u0997\u09cd\u09b2\u09cb\u09ac<\/strong><br \/>\n<a href=\"https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2018\/07\/The-Boston-Globe_A-pediatric-researcher-whose-son-died-of-progeria-sees-....pdf\" target=\"_blank\" rel=\"noopener noreferrer\"><em>\u098f\u0995\u099c\u09a8 \u09b6\u09bf\u09b6\u09c1\u09b0\u09cb\u0997 \u0997\u09ac\u09c7\u09b7\u0995 \u09af\u09be\u09b0 \u099b\u09c7\u09b2\u09c7 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09af\u09bc \u09ae\u09be\u09b0\u09be \u0997\u09c7\u099b\u09c7 \u09a4\u09bf\u09a8\u09bf \u09a8\u09a4\u09c1\u09a8 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be\u09b0 \u09aa\u09cd\u09b0\u09a4\u09bf\u09b6\u09cd\u09b0\u09c1\u09a4\u09bf \u09a6\u09c7\u0996\u09c7\u099b\u09c7\u09a8<\/em> \u098f\u09aa\u09cd\u09b0\u09bf\u09b2 24, 2018<\/a><\/li>\n<li><strong>\u09ac\u09cd\u09b0\u09be\u0989\u09a8 \u09a8\u09bf\u0989\u099c<\/strong><br \/>\n<a href=\"https:\/\/news.brown.edu\/articles\/2018\/04\/progeria\" target=\"_blank\" rel=\"noopener noreferrer\"><em>\u0997\u09ac\u09c7\u09b7\u09a3\u09be \u0985\u0995\u09be\u09b2 \u09ac\u09be\u09b0\u09cd\u09a7\u0995\u09cd\u09af \u09b0\u09cb\u0997\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u09aa\u09cd\u09b0\u09a4\u09bf\u09b6\u09cd\u09b0\u09c1\u09a4\u09bf\u09b6\u09c0\u09b2 \u09a1\u09cd\u09b0\u09be\u0997 \u09a5\u09c7\u09b0\u09be\u09aa\u09bf\u09b0 \u09aa\u09b0\u09be\u09ae\u09b0\u09cd\u09b6 \u09a6\u09c7\u09af\u09bc<\/em> \u098f\u09aa\u09cd\u09b0\u09bf\u09b2 24, 2018<\/a><\/li>\n<\/ul>\n<p><em>\u201c\u098f\u099f\u09bf \u098f\u09ae\u09a8 \u098f\u0995\u099f\u09bf \u0997\u09b2\u09cd\u09aa \u09af\u09be \u0985\u09a8\u09c7\u0995 \u09b8\u09cd\u09a4\u09b0\u09c7 \u0985\u09a8\u09c1\u09aa\u09cd\u09b0\u09c7\u09b0\u09a3\u09be\u09a6\u09be\u09af\u09bc\u0995\u0964 \u0996\u09c1\u09ac \u09ac\u09bf\u09b6\u09c7\u09b7 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u098f\u0995\u099f\u09bf \u0997\u09cd\u09b0\u09c1\u09aa\u09c7\u09b0 \u099c\u09c0\u09ac\u09a8 \u09aa\u09b0\u09bf\u09ac\u09b0\u09cd\u09a4\u09a8 \u0995\u09b0\u09be\u09b0 \u09b8\u09ae\u09cd\u09ad\u09be\u09ac\u09a8\u09be \u09b0\u09af\u09bc\u09c7\u099b\u09c7\u0964 \u0995\u09bf\u09a8\u09cd\u09a4\u09c1 \u098f\u099f\u09bf \u09b8\u09a0\u09bf\u0995\u09ad\u09be\u09ac\u09c7 \u099a\u09b2\u09c7 \u09af\u09be\u0993\u09af\u09bc\u09be \u09ac\u09c8\u099c\u09cd\u099e\u09be\u09a8\u09bf\u0995 \u09aa\u09a6\u09cd\u09a7\u09a4\u09bf\u09b0 \u0989\u09a6\u09be\u09b9\u09b0\u09a3\u0993 \u09ac\u099f\u09c7, \u09af\u09c7\u0996\u09be\u09a8\u09c7 \u0995\u09a0\u09cb\u09b0 \u09ae\u09cc\u09b2\u09bf\u0995 \u09ac\u09bf\u099c\u09cd\u099e\u09be\u09a8 \u098f\u09ac\u0982 \u098f\u0995\u099f\u09bf \u09ac\u09bf\u09a6\u09cd\u09af\u09ae\u09be\u09a8 \u0993\u09b7\u09c1\u09a7\u09c7\u09b0 \u098f\u0995\u099f\u09bf \u09b8\u09cd\u09ae\u09be\u09b0\u09cd\u099f \u09aa\u09cd\u09b0\u09af\u09bc\u09cb\u0997 \u09ae\u09bf\u09b2\u09bf\u09a4 \u09ab\u09b2\u09be\u09ab\u09b2 \u09a4\u09c8\u09b0\u09bf \u0995\u09b0\u09c7 \u09af\u09be \u09aa\u09cd\u09b0\u0995\u09c3\u09a4 \u09b8\u09be\u09ab\u09b2\u09cd\u09af\u0964&quot;<\/em><\/p>\n<p><em>\u2013 \u098f\u09ab. \u09aa\u09c7\u09b0\u09bf \u0989\u0987\u09b2\u09b8\u09a8 \u098f\u09ae\u09a1\u09bf, MSCE, \u0987\u09af\u09bc\u09c7\u09b2 \u09b8\u09cd\u0995\u09c1\u09b2 \u0985\u09ab \u09ae\u09c7\u09a1\u09bf\u09b8\u09bf\u09a8, \u09ae\u09c7\u09a1\u09aa\u09c7\u099c \u099f\u09c1\u09a1\u09c7<\/em><\/p>\n<p><strong>\u0995\u09bf\u09ad\u09be\u09ac\u09c7 \u0986\u09ae\u09b0\u09be \u098f\u0987 \u09ac\u09bf\u09b8\u09cd\u09ae\u09af\u09bc\u0995\u09b0 \u09a6\u09bf\u09a8 \u09aa\u09c7\u09a4\u09c7 \u09aa\u09be\u09b0\u09bf?<\/strong><br \/>\n\u0985\u09a8\u09c1\u09b8\u09b0\u09a3 <a href=\"https:\/\/www.progeriaresearch.org\/bn\/identification-of-gene-gives-hope-to-children-with-progeria\/\" target=\"_blank\" rel=\"noopener noreferrer\">2003 \u099c\u09bf\u09a8 \u09ae\u09bf\u0989\u099f\u09c7\u09b6\u09a8 \u0986\u09ac\u09bf\u09b7\u09cd\u0995\u09be\u09b0<\/a> \u09af\u09be\u09b0 \u0995\u09be\u09b0\u09a3\u09c7 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be, \u09aa\u09bf\u0986\u09b0\u098f\u09ab-\u0985\u09b0\u09cd\u09a5\u09be\u09af\u09bc\u09a8\u0995\u09c3\u09a4 \u0997\u09ac\u09c7\u09b7\u0995\u09b0\u09be \u099a\u09bf\u09b9\u09cd\u09a8\u09bf\u09a4 \u0995\u09b0\u09c7\u099b\u09c7\u09a8\u00a0<a href=\"https:\/\/www.progeriaresearch.org\/bn\/the-fti-drug\/\">\u098f\u09ab\u099f\u09bf\u0986\u0987<\/a>\u00a0\u098f\u0995\u099f\u09bf \u09b8\u09ae\u09cd\u09ad\u09be\u09ac\u09cd\u09af \u09a1\u09cd\u09b0\u09be\u0997 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be \u09b9\u09bf\u09b8\u09be\u09ac\u09c7\u0964 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be-\u09b8\u09c3\u09b7\u09cd\u099f\u09bf\u0995\u09be\u09b0\u09c0 \u09ae\u09bf\u0989\u099f\u09c7\u09b6\u09a8 \u09aa\u09cd\u09b0\u09cb\u099f\u09bf\u09a8 \u0989\u09ce\u09aa\u09be\u09a6\u09a8\u09c7\u09b0 \u09a6\u09bf\u0995\u09c7 \u09aa\u09b0\u09bf\u099a\u09be\u09b2\u09bf\u09a4 \u0995\u09b0\u09c7\u00a0<em>progerin<\/em>, \u09af\u09be \u0995\u09cb\u09b7\u09c7\u09b0 \u0995\u09be\u09b0\u09cd\u09af\u0995\u09be\u09b0\u09bf\u09a4\u09be\u0995\u09c7 \u0995\u09cd\u09b7\u09a4\u09bf\u0997\u09cd\u09b0\u09b8\u09cd\u09a4 \u0995\u09b0\u09c7\u0964 \u09b6\u09b0\u09c0\u09b0\u09c7\u09b0 \u0989\u09aa\u09b0 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09a8\u09c7\u09b0 \u09ac\u09bf\u09b7\u09be\u0995\u09cd\u09a4 \u09aa\u09cd\u09b0\u09ad\u09be\u09ac\u09c7\u09b0 \u098f\u0995\u099f\u09bf \u0985\u0982\u09b6 &quot;\u09ab\u09be\u09b0\u09a8\u09c7\u09b8\u09bf\u09b2 \u0997\u09cd\u09b0\u09c1\u09aa&quot; \u09a8\u09be\u09ae\u0995 \u098f\u0995\u099f\u09bf \u0985\u09a3\u09c1 \u09a6\u09cd\u09ac\u09be\u09b0\u09be \u09b8\u09c3\u09b7\u09cd\u099f \u09b9\u09af\u09bc, \u09af\u09be \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09a8 \u09aa\u09cd\u09b0\u09cb\u099f\u09bf\u09a8\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u09b8\u0982\u09af\u09c1\u0995\u09cd\u09a4 \u09a5\u09be\u0995\u09c7 \u098f\u09ac\u0982 \u098f\u099f\u09bf \u09b6\u09b0\u09c0\u09b0\u09c7\u09b0 \u0995\u09cb\u09b7\u0995\u09c7 \u0995\u09cd\u09b7\u09a4\u09bf\u0997\u09cd\u09b0\u09b8\u09cd\u09a4 \u0995\u09b0\u09a4\u09c7 \u09b8\u09be\u09b9\u09be\u09af\u09cd\u09af \u0995\u09b0\u09c7\u0964 \u098f\u09ab\u099f\u09bf\u0986\u0987\u0997\u09c1\u09b2\u09bf \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09a8\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u09ab\u09be\u09b0\u09cd\u09a8\u09c7\u09b8\u09be\u0987\u09b2 \u0997\u09cd\u09b0\u09c1\u09aa\u09c7\u09b0 \u09b8\u0982\u09af\u09c1\u0995\u09cd\u09a4\u09bf \u09ac\u09cd\u09b2\u0995 \u0995\u09b0\u09c7, \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09a8\u09c7\u09b0 \u0995\u09cd\u09b7\u09a4\u09bf\u09b0 \u0995\u09be\u09b0\u09a3\u0997\u09c1\u09b2\u09bf \u09b9\u09cd\u09b0\u09be\u09b8 \u0995\u09b0\u09c7 \u0995\u09be\u099c \u0995\u09b0\u09c7\u0964<\/p>\n<p><strong>\u0985\u09a7\u09cd\u09af\u09af\u09bc\u09a8\u09c7\u09b0 \u0986\u09b0\u0993 \u09ac\u09bf\u09b8\u09cd\u09a4\u09be\u09b0\u09bf\u09a4 \u099c\u09be\u09a8\u09be\u09b0 \u099c\u09a8\u09cd\u09af,\u00a0<a href=\"https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2018\/04\/PRF-JAMA-Announcement_Press-Release-1.pdf\">\u09aa\u09cd\u09b0\u09c7\u09b8 \u09b0\u09bf\u09b2\u09bf\u099c\u09c7\u09b0 \u099c\u09a8\u09cd\u09af \u098f\u0996\u09be\u09a8\u09c7 \u0995\u09cd\u09b2\u09bf\u0995 \u0995\u09b0\u09c1\u09a8<\/a> <\/strong><\/p>\n<p><em>\u201c\u098f\u0987 \u09ac\u09bf\u09b0\u09b2 \u09ae\u09be\u09b0\u09be\u09a4\u09cd\u09ae\u0995 \u09b0\u09cb\u0997\u09c7 \u0986\u0995\u09cd\u09b0\u09be\u09a8\u09cd\u09a4 \u09b6\u09bf\u09b6\u09c1\u09a6\u09c7\u09b0 \u098f\u0987 \u0995\u09cd\u09b7\u09c1\u09a6\u09cd\u09b0 \u099c\u09a8\u09b8\u0982\u0996\u09cd\u09af\u09be\u09b0 \u099a\u09bf\u0995\u09bf\u09a4\u09cd\u09b8\u09be\u09b0 \u0995\u09be\u09b0\u09cd\u09af\u0995\u09be\u09b0\u09bf\u09a4\u09be \u09aa\u09cd\u09b0\u09a6\u09b0\u09cd\u09b6\u09a8 \u0995\u09b0\u09be \u098f\u0995\u099f\u09bf \u09ac\u09a1\u09bc \u099a\u09cd\u09af\u09be\u09b2\u09c7\u099e\u09cd\u099c\u0964 \u098f\u0987\u09ad\u09be\u09ac\u09c7, \u0986\u09ae\u09bf \u098f\u0987 \u09b8\u09b0\u09cd\u09ac\u09b6\u09c7\u09b7 \u0985\u09a8\u09c1\u09b8\u09a8\u09cd\u09a7\u09be\u09a8 \u09a6\u09cd\u09ac\u09be\u09b0\u09be \u09ac\u09bf\u09b6\u09c7\u09b7\u09ad\u09be\u09ac\u09c7 \u0989\u09a4\u09cd\u09b8\u09be\u09b9\u09bf\u09a4\u0964&quot;<\/em><\/p>\n<p><em>\u2013 \u09a1\u09be\u0983 \u09ab\u09cd\u09b0\u09be\u09a8\u09cd\u09b8\u09bf\u09b8 \u0995\u09b2\u09bf\u09a8\u09cd\u09b8, \u09a8\u09cd\u09af\u09be\u09b6\u09a8\u09be\u09b2 \u0987\u09a8\u09b8\u09cd\u099f\u09bf\u099f\u09bf\u0989\u099f \u0985\u09ab \u09b9\u09c7\u09b2\u09a5 \u098f\u09b0 \u09a1\u09bf\u09b0\u09c7\u0995\u09cd\u099f\u09b0<\/em><\/p>\n<p><strong>\u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be \u09b8\u09be\u09a7\u09be\u09b0\u09a3 \u09ac\u09be\u09b0\u09cd\u09a7\u0995\u09cd\u09af \u09aa\u09cd\u09b0\u0995\u09cd\u09b0\u09bf\u09af\u09bc\u09be\u09b0 \u09b8\u09be\u09a5\u09c7 \u09af\u09c1\u0995\u09cd\u09a4<\/strong><a href=\"https:\/\/web-beta.archive.org\/web\/20170128050324\/https:\/www.progeriaresearch.org\/whats_new_in_progeria_research.html#2\"><br \/>\n<\/a>\u0997\u09ac\u09c7\u09b7\u09a3\u09be\u09af\u09bc \u09a6\u09c7\u0996\u09be \u0997\u09c7\u099b\u09c7 \u09af\u09c7 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be-\u09b8\u09c3\u09b7\u09cd\u099f\u09bf\u0995\u09be\u09b0\u09c0 \u09aa\u09cd\u09b0\u09cb\u099f\u09bf\u09a8\u00a0<em>progerin<\/em>\u00a0\u098f\u099b\u09be\u09a1\u09bc\u09be\u0993 \u09b8\u09be\u09a7\u09be\u09b0\u09a3 \u099c\u09a8\u09b8\u0982\u0996\u09cd\u09af\u09be\u09b0 \u09ae\u09a7\u09cd\u09af\u09c7 \u0989\u09a4\u09cd\u09aa\u09be\u09a6\u09bf\u09a4 \u09b9\u09af\u09bc \u098f\u09ac\u0982 \u09ac\u09af\u09bc\u09b8\u09c7\u09b0 \u09b8\u09be\u09a5\u09c7 \u09ac\u09c3\u09a6\u09cd\u09a7\u09bf \u09aa\u09be\u09af\u09bc\u0964 \u0997\u09ac\u09c7\u09b7\u0995\u09b0\u09be \u098f\u09ab\u099f\u09bf\u0986\u0987-\u098f\u09b0 \u09aa\u09cd\u09b0\u09ad\u09be\u09ac \u0985\u09a8\u09cd\u09ac\u09c7\u09b7\u09a3 \u099a\u09be\u09b2\u09bf\u09af\u09bc\u09c7 \u09af\u09be\u0993\u09af\u09bc\u09be\u09b0 \u09aa\u09b0\u09bf\u0995\u09b2\u09cd\u09aa\u09a8\u09be \u0995\u09b0\u09c7\u099b\u09c7\u09a8, \u09af\u09be \u09ac\u09bf\u099c\u09cd\u099e\u09be\u09a8\u09c0\u09a6\u09c7\u09b0 \u0995\u09be\u09b0\u09cd\u09a1\u09bf\u0993\u09ad\u09be\u09b8\u0995\u09c1\u09b2\u09be\u09b0 \u09b0\u09cb\u0997 \u09b8\u09ae\u09cd\u09aa\u09b0\u09cd\u0995\u09c7 \u0986\u09b0\u0993 \u099c\u09be\u09a8\u09a4\u09c7 \u09b8\u09be\u09b9\u09be\u09af\u09cd\u09af \u0995\u09b0\u09a4\u09c7 \u09aa\u09be\u09b0\u09c7 \u09af\u09be \u09b2\u0995\u09cd\u09b7 \u09b2\u0995\u09cd\u09b7 \u09ae\u09be\u09a8\u09c1\u09b7\u0995\u09c7 \u09aa\u09cd\u09b0\u09ad\u09be\u09ac\u09bf\u09a4 \u0995\u09b0\u09c7, \u09b8\u09c7\u0987\u09b8\u09be\u09a5\u09c7 \u09b8\u09be\u09a7\u09be\u09b0\u09a3 \u09ac\u09be\u09b0\u09cd\u09a7\u0995\u09cd\u09af \u09aa\u09cd\u09b0\u0995\u09cd\u09b0\u09bf\u09af\u09bc\u09be \u09af\u09be \u0986\u09ae\u09be\u09a6\u09c7\u09b0 \u09b8\u0995\u09b2\u0995\u09c7 \u09aa\u09cd\u09b0\u09ad\u09be\u09ac\u09bf\u09a4 \u0995\u09b0\u09c7\u0964<\/p>\n<p><strong>\u09b8\u09ac\u09be\u0987\u0995\u09c7 \u09a7\u09a8\u09cd\u09af\u09ac\u09be\u09a6-<\/strong>\u00a0<strong>\u0986\u09ae\u09b0\u09be \u09a4\u09cb\u09ae\u09be\u0995\u09c7 \u099b\u09be\u09a1\u09bc\u09be \u098f\u099f\u09be \u0995\u09b0\u09a4\u09c7 \u09aa\u09be\u09b0\u09a4\u09be\u09ae \u09a8\u09be!<\/strong><br \/>\n\u0986\u09ae\u09b0\u09be \u098f\u0987 \u09af\u09c1\u0997\u09be\u09a8\u09cd\u09a4\u0995\u09be\u09b0\u09c0 \u09ab\u09b2\u09be\u09ab\u09b2\u0997\u09c1\u09b2\u09bf \u0985\u09b0\u09cd\u099c\u09a8 \u0995\u09b0\u09be\u09b0 \u09aa\u09cd\u09b0\u09a7\u09be\u09a8 \u0995\u09be\u09b0\u09a3\u0997\u09c1\u09b2\u09bf\u09b0 \u09ae\u09a7\u09cd\u09af\u09c7 \u098f\u0995\u099f\u09bf \u09b9\u09b2 \u09aa\u09cd\u09b0\u099a\u09c1\u09b0 \u09b8\u09ae\u09b0\u09cd\u09a5\u0995 \u09af\u09be\u09b0\u09be \u09a4\u09b9\u09ac\u09bf\u09b2 \u098f\u09ac\u0982 \u0985\u09a8\u09cd\u09af\u09be\u09a8\u09cd\u09af \u09b8\u09b9\u09be\u09af\u09bc\u09a4\u09be \u09aa\u09cd\u09b0\u09a6\u09be\u09a8 \u0995\u09b0\u09c7\u099b\u09c7, \u0986\u09ae\u09be\u09a6\u09c7\u09b0 \u099a\u09c2\u09a1\u09bc\u09be\u09a8\u09cd\u09a4 \u09b2\u0995\u09cd\u09b7\u09cd\u09af \u0985\u09b0\u09cd\u099c\u09a8\u09c7\u09b0 \u098f\u0995 \u09a7\u09be\u09aa \u0995\u09be\u099b\u09be\u0995\u09be\u099b\u09bf \u09af\u09c7\u09a4\u09c7 \u09b8\u09be\u09b9\u09be\u09af\u09cd\u09af \u0995\u09b0\u09c7\u099b\u09c7 \u2013 \u09aa\u09cd\u09b0\u09cb\u099c\u09c7\u09b0\u09bf\u09af\u09bc\u09be\u09b0 \u09a8\u09bf\u09b0\u09be\u09ae\u09af\u09bc\u0964<\/p>","protected":false},"excerpt":{"rendered":"<p>April 24, 2018: A new study published in The Journal of the American Medical Association (JAMA) reports that lonafarnib, a farnesyltransferase inhibitor (FTI), helped extend survival in children with Progeria. Authors from Boston Children\u2019s Hospital and Brown University tracked more than 250 children from six continents to demonstrate a link between lonafarnib treatment and extended [&hellip;]<\/p>\n","protected":false},"author":2,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_et_pb_use_builder":"","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":"","_links_to":"","_links_to_target":""},"class_list":["post-4004","page","type-page","status-publish","hentry"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>First Ever | The Progeria Research Foundation<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.progeriaresearch.org\/bn\/first-ever-demonstrate-survival-benefit-in-progeria\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"First Ever | The Progeria Research Foundation\" \/>\n<meta property=\"og:description\" content=\"April 24, 2018: A new study published in The Journal of the American Medical Association (JAMA) reports that lonafarnib, a farnesyltransferase inhibitor (FTI), helped extend survival in children with Progeria. 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