{"id":19721,"date":"2024-11-27T17:23:42","date_gmt":"2024-11-27T22:23:42","guid":{"rendered":"https:\/\/www.progeriaresearch.org\/?page_id=19721"},"modified":"2024-12-02T12:37:36","modified_gmt":"2024-12-02T17:37:36","slug":"progerinin_trial","status":"publish","type":"page","link":"https:\/\/www.progeriaresearch.org\/de\/progerinin_trial\/","title":{"rendered":"Jetzt anmelden: Neue Informationen zu klinischen Studien"},"content":{"rendered":"<p>[et_pb_section fb_built=&#8221;1&#8243; fullwidth=&#8221;on&#8221; disabled_on=&#8221;off|off|off&#8221; _builder_version=&#8221;4.16&#8243; border_width_bottom=&#8221;55px&#8221; border_color_bottom=&#8221;#29327a&#8221; locked=&#8221;off&#8221; collapsed=&#8221;off&#8221; global_colors_info=&#8221;{}&#8221;][et_pb_fullwidth_header _builder_version=&#8221;4.27.2&#8243; title_font=&#8221;||||||||&#8221; title_font_size=&#8221;55&#8243; background_color=&#8221;#29327a&#8221; background_image=&#8221;https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2023\/06\/header-Mio-Map-1-Dec-2017.jpg&#8221; background_position=&#8221;center_left&#8221; custom_padding=&#8221;7vw||7vw||true|&#8221; custom_padding_tablet=&#8221;&#8221; custom_padding_phone=&#8221;|56px||&#8221; custom_padding_last_edited=&#8221;on|desktop&#8221; title_font_size_tablet=&#8221;45px&#8221; title_font_size_phone=&#8221;40px&#8221; title_font_size_last_edited=&#8221;on|phone&#8221; z_index_tablet=&#8221;500&#8243; custom_css_main_element=&#8221;background-position: center 18% !important;&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<h1><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><span style=\"color: #000080;\"><b><i><\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: right;\"><\/h1>\n<h1 style=\"text-align: left;\"><span style=\"color: #000080;\"><b><i>Jetzt anmelden: <\/i><\/b><\/span><\/h1>\n<h1 style=\"text-align: left;\"><span style=\"color: #000080;\"><b><i>Neue Informationen zu klinischen Studien<\/i><\/b><\/span><\/h1>\n<p>[\/et_pb_fullwidth_header][\/et_pb_section][et_pb_section fb_built=&#8221;1&#8243; use_custom_gutter=&#8221;on&#8221; gutter_width=&#8221;1&#8243; specialty=&#8221;on&#8221; padding_left_1=&#8221;35px&#8221; padding_left_2=&#8221;35px&#8221; padding_2_tablet=&#8221;|||0px&#8221; padding_2_phone=&#8221;|||0px&#8221; padding_2_last_edited=&#8221;on|desktop&#8221; module_class_1=&#8221;sidebar-secondary-nav&#8221; module_class=&#8221;handprint-bg&#8221; _builder_version=&#8221;4.27.2&#8243; background_image=&#8221;https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2019\/04\/blue-handprint-only.png&#8221; parallax=&#8221;on&#8221; parallax_method=&#8221;off&#8221; inner_width=&#8221;100%&#8221; inner_max_width=&#8221;100%&#8221; custom_padding=&#8221;0|0px|54px|0px|false|false&#8221; z_index_tablet=&#8221;500&#8243; border_width_top=&#8221;10px&#8221; border_color_top=&#8221;#8fd2ed&#8221; use_custom_width=&#8221;on&#8221; width_unit=&#8221;off&#8221; custom_width_percent=&#8221;100%&#8221; global_colors_info=&#8221;{}&#8221;][et_pb_column type=&#8221;1_4&#8243; _builder_version=&#8221;4.16&#8243; custom_padding=&#8221;|||&#8221; global_colors_info=&#8221;{}&#8221; custom_padding__hover=&#8221;|||&#8221;][et_pb_sidebar area=&#8221;et_pb_widget_area_1&#8243; disabled_on=&#8221;on|on|off&#8221; admin_label=&#8221;Science Sidebar&#8221; module_class=&#8221;subpage-sidebars&#8221; _builder_version=&#8221;4.16&#8243; animation_style=&#8221;fade&#8221; z_index_tablet=&#8221;500&#8243; header_text_shadow_horizontal_length_tablet=&#8221;0px&#8221; header_text_shadow_vertical_length_tablet=&#8221;0px&#8221; header_text_shadow_blur_strength_tablet=&#8221;1px&#8221; body_text_shadow_horizontal_length_tablet=&#8221;0px&#8221; body_text_shadow_vertical_length_tablet=&#8221;0px&#8221; body_text_shadow_blur_strength_tablet=&#8221;1px&#8221; border_width_right=&#8221;5px&#8221; border_width_right_tablet=&#8221;5px&#8221; border_width_right_phone=&#8221;5px&#8221; box_shadow_horizontal_tablet=&#8221;0px&#8221; box_shadow_vertical_tablet=&#8221;0px&#8221; box_shadow_blur_tablet=&#8221;40px&#8221; 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custom_padding=&#8221;|||&#8221; global_colors_info=&#8221;{}&#8221; custom_padding__hover=&#8221;|||&#8221;][et_pb_text admin_label=&#8221;New Clinical Trial Information For Families and Their Physicians &#8221; _builder_version=&#8221;4.27.2&#8243; text_font_size=&#8221;18px&#8221; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; custom_margin=&#8221;||28px|||&#8221; hover_enabled=&#8221;0&#8243; z_index_tablet=&#8221;500&#8243; box_shadow_horizontal_tablet=&#8221;0px&#8221; box_shadow_vertical_tablet=&#8221;0px&#8221; box_shadow_blur_tablet=&#8221;40px&#8221; box_shadow_spread_tablet=&#8221;0px&#8221; global_colors_info=&#8221;{}&#8221; sticky_enabled=&#8221;0&#8243;]<\/p>\n<h4 style=\"text-align: center;\"><strong><em>2. Dezember 2024 Beitrag:<\/em><\/strong><\/h4>\n<h4 style=\"text-align: center;\"><strong><em>Neue Informationen zu klinischen Studien f\u00fcr Familien und ihre \u00c4rzte<\/em><\/strong><\/h4>\n<h4 style=\"text-align: center;\"><em><strong><\/strong><\/em><\/h4>\n<h4 style=\"text-align: center;\"><em><strong>Die Anmeldung zur neuen klinischen Progerinin-Studie hat begonnen<\/strong><\/em><\/h4>\n<p>Die Anmeldung f\u00fcr die Progerininstudie ist jetzt ge\u00f6ffnet! Der Titel dieser Forschungsstudie lautet: Eine randomisierte, offene Phase-2a-Studie zur Bestimmung der optimalen Dosis und Bewertung der Sicherheit, Vertr\u00e4glichkeit und Pharmakokinetik von Progerinin bei Patienten mit Hutchinson-Gilford-Progerie-Syndrom (HGPS). Der Studienort ist das Boston Children&#039;s Hospital (BCH). Der Studiensponsor ist das in Korea ans\u00e4ssige Unternehmen PRG Science &amp; Technology (PRG S&amp;T). PRF arbeitet bei dieser Studie mit BCH und PRG S&amp;T zusammen. Im Rahmen der Zusammenarbeit wird PRF die An- und Abreise zum Studienort in Boston sowie die Unterbringung w\u00e4hrend des Aufenthalts in Boston organisieren. Informationen zur Studie werden auch auf der Website ver\u00f6ffentlicht. <a href=\"https:\/\/clinicaltrials.gov\/\">clinicaltrials.gov<\/a><\/p>\n<p>[\/et_pb_text][et_pb_text admin_label=&#8221;Information For Patients with Progeria and their Doctors&#8221; _builder_version=&#8221;4.27.2&#8243; text_text_color=&#8221;#000000&#8243; text_font_size=&#8221;18px&#8221; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; custom_margin=&#8221;||19px|||&#8221; z_index_tablet=&#8221;500&#8243; box_shadow_horizontal_tablet=&#8221;0px&#8221; box_shadow_vertical_tablet=&#8221;0px&#8221; box_shadow_blur_tablet=&#8221;40px&#8221; box_shadow_spread_tablet=&#8221;0px&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<h5><strong><em>Informationen f\u00fcr Patienten mit Progerie und ihre \u00c4rzte<\/em><\/strong><\/h5>\n<ul>\n<li>Bei dieser Forschungsstudie geht es um ein neues Pr\u00fcfpr\u00e4parat namens Progerinin, das zus\u00e4tzlich zu Lonafarnib eingenommen werden kann.<\/li>\n<li>Die Sicherheit und\/oder Wirksamkeit von Progerinin zur Behandlung von Progerie (HGPS) konnte bisher nicht nachgewiesen werden, und der Verkauf von Progerinin ist von der FDA oder anderen internationalen Beh\u00f6rden noch nicht zugelassen.<\/li>\n<li>Das Ziel dieser Studie besteht darin, die Nebenwirkungen von Progerinin und die optimale Dosierung zu bestimmen und zu pr\u00fcfen, ob Progerinin bei der Behandlung von Patienten mit Progerie helfen kann.<\/li>\n<li>Progerinin zeigte Vorteile, als Wissenschaftler es an Progeria-Zellen und Progeria-M\u00e4usen testeten. Es wurde Erwachsenen ohne Progerie entweder einmalig (eine Dosis) oder f\u00fcr einige Wochen verabreicht. Kindern und jungen Erwachsenen mit Progerie wurde es nie verabreicht.<\/li>\n<li>Progerinin wird als in Wasser gel\u00f6stes Pulver verabreicht und zweimal t\u00e4glich eingenommen.<\/li>\n<li>Das Studienteam geht davon aus, dass zwischen 10 und 16 Kinder und junge Erwachsene in die Studie aufgenommen werden, die die im Studienprotokoll festgelegten spezifischen Aufnahmekriterien erf\u00fcllen. Die Aufnahme beginnt mit 10 Kindern und jungen Erwachsenen mit Progerie (HGPS).<\/li>\n<li>8 Studienteilnehmer nehmen Progerinin zweimal t\u00e4glich oral ein und nehmen au\u00dferdem wie gewohnt Lonafarnib ein; 2 Teilnehmer nehmen kein Progerinin, sondern weiterhin Lonafarnib ein. Das Studienteam wird erst wissen, welche Patienten in der Progerinin-Behandlungsgruppe oder der Lonafarnib-Gruppe sind, wenn ein Computer sie zuf\u00e4llig zuweist.<\/li>\n<\/ul>\n<p>[\/et_pb_text][et_pb_text admin_label=&#8221;If patient bullet 8&#8243; _builder_version=&#8221;4.27.2&#8243; text_text_color=&#8221;#000000&#8243; text_font_size=&#8221;18px&#8221; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; min_height=&#8221;338px&#8221; custom_margin=&#8221;||-7px|||&#8221; custom_padding=&#8221;||0px|||&#8221; z_index_tablet=&#8221;500&#8243; box_shadow_horizontal_tablet=&#8221;0px&#8221; box_shadow_vertical_tablet=&#8221;0px&#8221; box_shadow_blur_tablet=&#8221;40px&#8221; box_shadow_spread_tablet=&#8221;0px&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<ul>\n<li>Wenn einem Patienten Progerinin zusammen mit seiner \u00fcblichen Lonafarnib-Dosis verschrieben wird:\n<ul>\n<li style=\"list-style-type: none;\">\n<ul>\n<li>Der Patient muss viermal nach Boston reisen, um sich testen zu lassen (4 Monate zwischen den Besuchen). Das bedeutet, dass der Patient f\u00fcr seinen ersten Besuch nach Boston reist, 4 Monate nach dem ersten Besuch wiederkommt, dann 8 Monate nach dem ersten Besuch und schlie\u00dflich 12 Monate nach dem ersten Besuch.<\/li>\n<li>Die erste Dosis Progerinin ist eine Anfangsdosis. Zwischen den ersten beiden Besuchen in Boston muss der Patient zu Hause bleiben, w\u00e4hrend er diese erste Dosis erh\u00e4lt. Der Patient wird an den Tagen 7, 14 und 28 sowie im zweiten und dritten Monat Kontrollanrufe oder Zoom-Anrufe mit dem BCH-Studienteam f\u00fchren. Diese Anrufe dienen der \u00dcberwachung etwaiger Nebenwirkungen von Progerinin. Der Patient wird auch in engem Kontakt mit dem BCH-Studienteam stehen, falls zwischen den Anrufen Nebenwirkungen auftreten.<\/li>\n<li>Zwischen den Besuchen in Boston werden die Patienten vor Ort an ihrem Wohnort Bluttests unterzogen. Diese werden zwischen BCH und dem Hausarzt des Patienten in der zweiten und vierten Woche sowie im zweiten und dritten Monat vereinbart. Das Blut wird dem Patienten aus dem Arm entnommen und die Gesamtmenge, die bei jedem Besuch ben\u00f6tigt wird, betr\u00e4gt etwa einen halben Teel\u00f6ffel (2,5 ml). Die Ergebnisse dieser Tests werden von der Hausarztpraxis des Patienten an das BCH-Studienteam gesendet.<\/li>\n<\/ul>\n<p>[\/et_pb_text][et_pb_text admin_label=&#8221;If patient bullet 9&#8243; _builder_version=&#8221;4.27.2&#8243; text_text_color=&#8221;#000000&#8243; text_font_size=&#8221;18px&#8221; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; z_index_tablet=&#8221;500&#8243; box_shadow_horizontal_tablet=&#8221;0px&#8221; box_shadow_vertical_tablet=&#8221;0px&#8221; box_shadow_blur_tablet=&#8221;40px&#8221; box_shadow_spread_tablet=&#8221;0px&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<ul>\n<li>Wenn einem Patienten nur Lonafarnib verschrieben wird:\n<ul>\n<li style=\"list-style-type: none;\">\n<ul>\n<li style=\"text-align: left;\">Der Patient wird Boston zweimal besuchen, zu Beginn und im 12. Monat.<\/li>\n<li style=\"text-align: left;\">Der Patient kann 4 Monate nach Beginn der Studie vor Ort zu Hause eine Blutprobe abgeben. BCH und der \u00f6rtliche Arzt des Patienten werden die Entnahme dieser Blutprobe veranlassen.<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<\/li>\n<li>Drei\u00dfig Tage nach dem letzten pers\u00f6nlichen Besuch werden alle Probanden gebeten, ein weiteres Telefongespr\u00e4ch mit dem BCH-Studienteam zu f\u00fchren.<\/li>\n<li>Jeder Patient kann selbst entscheiden, ob er an der Studie teilnehmen m\u00f6chte oder nicht. Die Teilnahme an der klinischen Studie ist v\u00f6llig freiwillig.<\/li>\n<\/ul>\n<p>Wenn Sie mehr erfahren m\u00f6chten oder Interesse daran haben, von BCH bez\u00fcglich der Teilnahme an der Studie kontaktiert zu werden, wenden Sie sich bitte an die Progeria Research Foundation und wir werden Sie mit dem BCH-Studienteam in Verbindung setzen.<\/p>\n<p>Shelby Phillips, Koordinatorin f\u00fcr Patientenprogramme, The Progeria Research Foundation<br \/>E-Mail: <a href=\"mailto:sphillips@progeriaresearch.org\">sphillips@progeriaresearch.org<\/a><\/p>\n<p>Mobiltelefon f\u00fcr WhatsApp, Telegram, WeChat: 1-987-876-2407<br \/>B\u00fcrotelefon: 988-548-5308<\/p>\n<p>Beste gr\u00fc\u00dfe,<br \/>Shelby Phillips, Koordinatorin f\u00fcr Patientenprogramme und<br \/>Dr. Leslie Gordon, \u00c4rztliche Direktorin<br \/>Die Progeria Research Foundation<\/p>\n<p>[\/et_pb_text][\/et_pb_column_inner][\/et_pb_row_inner][\/et_pb_column][\/et_pb_section][et_pb_section fb_built=\u201d1\u2033 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Enrollment is now open for the progerinin trial! The title of this research study is: A Phase 2a, Randomized, Open-Label Study to Determine the Optimal Dose and [&hellip;]<\/p>","protected":false},"author":2,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":"","_links_to":"","_links_to_target":""},"class_list":["post-19721","page","type-page","status-publish","hentry"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v26.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Progerinin trial | The Progeria Research Foundation<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.progeriaresearch.org\/de\/progerinin_trial\/\" \/>\n<meta property=\"og:locale\" content=\"de_DE\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Progerinin trial | The Progeria Research Foundation\" \/>\n<meta property=\"og:description\" content=\"Enrolling Now: New Clinical Trial Information December 2, 2024 Posting: New Clinical Trial Information For Families and Their Physicians Enrollment in The New Progerinin Clinical Trial Has Begun Enrollment is now open for the progerinin trial! 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