{"id":18802,"date":"2024-07-24T12:33:03","date_gmt":"2024-07-24T16:33:03","guid":{"rendered":"https:\/\/www.progeriaresearch.org\/?p=18802"},"modified":"2025-01-29T09:22:01","modified_gmt":"2025-01-29T14:22:01","slug":"nytarticle2024","status":"publish","type":"post","link":"https:\/\/www.progeriaresearch.org\/nl\/2024\/07\/24\/nytarticle2024\/","title":{"rendered":"New York Times | 24 juli 2024: Een remedie voor progeria zou in het verschiet kunnen liggen"},"content":{"rendered":"<p>[et_pb_section fb_built=&#8221;1&#8243; _builder_version=&#8221;4.16&#8243; global_colors_info=&#8221;{}&#8221;][et_pb_row _builder_version=&#8221;4.16&#8243; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; global_colors_info=&#8221;{}&#8221;][et_pb_column type=&#8221;4_4&#8243; _builder_version=&#8221;4.16&#8243; custom_padding=&#8221;|||&#8221; global_colors_info=&#8221;{}&#8221; custom_padding__hover=&#8221;|||&#8221;][et_pb_image src=&#8221;https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2024\/05\/NYTarticle.png&#8221; title_text=&#8221;NYTarticle&#8221; url=&#8221;https:\/\/www.charitynavigator.org\/ein\/043460220&#8243; align=&#8221;center&#8221; admin_label=&#8221;NYT Article photo&#8221; _builder_version=&#8221;4.24.3&#8243; _module_preset=&#8221;default&#8221; width=&#8221;50%&#8221; max_width=&#8221;50%&#8221; global_colors_info=&#8221;{}&#8221;][\/et_pb_image][et_pb_image src=&#8221;https:\/\/www.progeriaresearch.org\/wp-content\/uploads\/2024\/05\/NY-Times-headline-screen-shot.png&#8221; align=&#8221;center&#8221; _builder_version=&#8221;4.24.3&#8243; _module_preset=&#8221;default&#8221; global_colors_info=&#8221;{}&#8221;][\/et_pb_image][et_pb_text _builder_version=&#8221;4.24.3&#8243; text_font_size=&#8221;18px&#8221; background_size=&#8221;initial&#8221; background_position=&#8221;top_left&#8221; background_repeat=&#8221;repeat&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<p>In een <a href=\"https:\/\/7fingzbab.cc.rs6.net\/tn.jsp?f=001reQqCYzvcBCiiYncnANHIp1b21gDgzdxTtqEICpY6m8QdjuewEPq7xIGbPejWj4M6E04x75sMymSNxUi2ayaeVHFSYvCh9HnXt0qPy5MovnVHFAlYX2vRwvBk430UfuBrPINGxb8cg96d0ksHvc6rLSK3alQ-U9PCTx8LpPG3gJZkAVTSo3u8UBhizzg-Y3biymquqUc9rA_iNA1Kk90h7B9j1S32TMxLtFikXptmiWYt49XxIHPXU4MpHPmrf-P_9ibXvSA2qxS_WeaCw5rYKQxKZdWk65AEKCMxuG0YiwEvsCOwmEc006WKD9hxpjBdfRiFqy5iHAiNtWtABdFcEgrjtc5-pZoef81KTI6Yi58ALhWH0vsHMhE9QHi0aNomGKIKPYxRRuGeqfwmsw5wG0PHfzXAiI4h4OuqA3C5bajkKNcNeYqa1jFi_Ixe_0iyNRbESsYKZw3EIXKJt0LAX-XyYopECL8zJTmpJIYUKmK3B5Jez0fKdcrzNIaMGLKHnTNsEkCSGt0e_ucNgqWphVVJlMKO7andrVdicS6CEGmGShaaamE0th3_au5V86A8QsT7bSIr_r2g-EZVWqq8y_ZTY_G0j959B02QvPAxVRs8J67QBZq7lfPwcpr5PWAmhVe7wbjDT5Xgexr1CrFzmwNIn0r0k3LvuT94Wb75cQ=&amp;c=6-5Yuj2121JvsJ-RDrfI1O5tQavJJdsWckWNUAmoE6Xn_h1l7he5Fg==&amp;ch=UQVNHEXTkcJwi1ZO8FoepARdvYUNKCB-9c2acQ6UT00JPkAW8eKG4Q==\"><strong>artikel vandaag gepubliceerd in de New York Times<\/strong><\/a>Dr. Leslie Gordon, medisch directeur van PRF, en collega&#039;s deelden het fenomenale verhaal van wetenschappelijke samenwerkingen die leidden tot recente doorbraken in genetische bewerking bij Progeria.<\/p>\n<p>Samenwerkingen met PRF&#039;s oude vrienden en collega&#039;s, voormalig NIH-directeur Dr. Francis Collins en genbewerkingsexpert Dr. David Liu van Harvard\/MIT, hebben tot buitengewone bevindingen geleid die eerder zijn gepubliceerd. <a href=\"https:\/\/7fingzbab.cc.rs6.net\/tn.jsp?f=001reQqCYzvcBCiiYncnANHIp1b21gDgzdxTtqEICpY6m8QdjuewEPq7xIGbPejWj4MFT4ah30FgI1TPUoL9uVnYLBTl83clppaj-8deQsQs00aIJ4GD6jHAhHBLdJc0vYwMeIpvvACOXdsDBRDiolPiVhEzhl7tkrz1qPkTay8MvCrXdYs38k8XrfxEKneYF0zeSbMSmkB0In-vK1Fqhj9aLSKe0vTWSElceJw9Wvd1yGnatxmz1l2q0PYoAHHLQAx&amp;c=6-5Yuj2121JvsJ-RDrfI1O5tQavJJdsWckWNUAmoE6Xn_h1l7he5Fg==&amp;ch=UQVNHEXTkcJwi1ZO8FoepARdvYUNKCB-9c2acQ6UT00JPkAW8eKG4Q==\"><strong>gepubliceerd in het tijdschrift <\/strong><\/a><a href=\"https:\/\/7fingzbab.cc.rs6.net\/tn.jsp?f=001reQqCYzvcBCiiYncnANHIp1b21gDgzdxTtqEICpY6m8QdjuewEPq7xIGbPejWj4MFT4ah30FgI1TPUoL9uVnYLBTl83clppaj-8deQsQs00aIJ4GD6jHAhHBLdJc0vYwMeIpvvACOXdsDBRDiolPiVhEzhl7tkrz1qPkTay8MvCrXdYs38k8XrfxEKneYF0zeSbMSmkB0In-vK1Fqhj9aLSKe0vTWSElceJw9Wvd1yGnatxmz1l2q0PYoAHHLQAx&amp;c=6-5Yuj2121JvsJ-RDrfI1O5tQavJJdsWckWNUAmoE6Xn_h1l7he5Fg==&amp;ch=UQVNHEXTkcJwi1ZO8FoepARdvYUNKCB-9c2acQ6UT00JPkAW8eKG4Q==\"><strong><em>Natuur<\/em><\/strong><\/a>, over de potentieel helende krachten van basisbewerking.<\/p>\n<p><strong>Het volledige verhaal leest u hier: <em><a href=\"https:\/\/www.nytimes.com\/2024\/07\/24\/health\/progeria-dna-base-editing.html?unlocked_article_code=1.9k0.YQ2f.8W0j5y_GhFC1&amp;smid=url-share2acQ6UT00JPkAW8eKG4Q==\">Een ziekte die kinderen snel ouder maakt, komt dichter bij een genezing<\/a><\/em><\/strong><\/p>\n<p>[\/et_pb_text][et_pb_testimonial quote_icon_color=&#8221;#8FD2ED&#8221; quote_icon_background_color=&#8221;#29327A&#8221; _builder_version=&#8221;4.27.0&#8243; _module_preset=&#8221;default&#8221; body_font_size=&#8221;20px&#8221; background_color=&#8221;#00B2E2&#8243; background_layout=&#8221;dark&#8221; custom_margin=&#8221;||25px||false|false&#8221; custom_padding=&#8221;0px||0px||false|false&#8221; border_radii=&#8221;on|40px|40px|40px|40px&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<p><strong><em><\/em><\/strong><\/p>\n<p><strong><em>De nieuwe vormen van genbewerking zijn \u201cpotentieel het antwoord op een droom die we allemaal willen laten uitkomen,\u201d<\/em><\/strong><\/p>\n<p><strong><em>Dokter Francis Collins<\/em><\/strong><\/p>\n<p>[\/et_pb_testimonial][et_pb_testimonial quote_icon_color=&#8221;#8FD2ED&#8221; quote_icon_background_color=&#8221;#29327A&#8221; _builder_version=&#8221;4.27.0&#8243; _module_preset=&#8221;default&#8221; body_font_size=&#8221;20px&#8221; background_color=&#8221;#00B2E2&#8243; background_layout=&#8221;dark&#8221; custom_margin=&#8221;||0px||false|false&#8221; custom_padding=&#8221;0px||0px||false|false&#8221; border_radii=&#8221;on|40px|40px|40px|40px&#8221; global_colors_info=&#8221;{}&#8221;]<\/p>\n<p><strong><em><\/em><\/strong><\/p>\n<p><b>Bekijk enkele van de geweldige reacties van lezers:<\/b><\/p>\n<p><em>\u201cDNA-bewerking, splicing en herschrijftechnologie\u2026 gewoon een verbijsterende lectuur. Wauw\u2026\u201d<\/em><\/p>\n<p><em>\u201cVoor een beter begrip van deze ziekte, kijk de film \u201cLife According to Sam\u201d op HBO. Je zult versteld staan van de toewijding van Sams ouders om een remedie voor progeria te ontdekken. Je zult versteld staan van Sam, die ik het geluk had te leren kennen toen hij het spelen van pauken in het symfonieorkest ontdekte tijdens een zomerkamp. Hij was een betrokken, nieuwsgierige multigetalenteerde student die zoveel heeft bereikt in zijn te korte leven.\u201d<\/em><\/p>\n<p><em>\u201cInspirerend artikel! Dank u wel, Times-verslaggever, dat u onze aandacht vestigt op de gevechten die het waard zijn om te vechten! De goede gevechten! Laten we de oorlog verklaren aan ziekte en wanorde in plaats van mens tegen mens. Stop geld in het doden van virussen, niet in elkaar. Blijf ons alstublieft bewuster maken van alle goede gevechten die in laboratoria en ziekenhuizen worden uitgevochten. We hebben het nodig! Dank u wel!\u201d<\/em><\/p>\n<p><em>\u201cZo ontroerend om te lezen. Dr. Collins is een Amerikaanse held. Deze wetenschappers op het randje hier verdienen onze financiering en onze bewondering. De pati\u00ebnten verdienen vooral onze steun. Wat een dappere groep mensen om met deze slopende ziekte te leven. Ik hoop op een grote doorbraak binnenkort.\u201d<\/em><\/p>\n<p><em>\u201cIk vond dit artikel geweldig! Bedankt NYT. Wat geweldig om te lezen over iets zo veelbelovends dat zoveel mensen zal helpen. Bravo voor Dr. Collins en collega&#039;s.\u201d<\/em><\/p>\n<p><em>\u201cWat een prachtig artikel en wat een Amerikaanse schat zijn Francis Collins en David Liu. Zo dankbaar voor hun onbaatzuchtige toewijding aan deze zeldzame genetische ziektes.\u201d<\/em><\/p>\n<p><em>\u201cAbsoluut fascinerend. Ik hoop dat ze snel goedkeuring krijgen voor de klinische proef. Geweldig werk.\u201d<\/em><\/p>\n<p><em>\u201cDit is gewoon fenomenaal. Ik was als kind erg ge\u00efnteresseerd in medicijnen en ik keek documentaires over allerlei zeldzame ziektes. Progeria viel me altijd op. Ik ben opgetogen dat dit soort werk wordt gedaan. Ik hoop dat dit succesvol is in het genezen van de kinderen die deze aandoening hebben en dat het gebruikt kan worden om nog veel meer kinderen te genezen.\u201d<\/em><\/p>\n<p><em>\u201cIn de jaren 90 was ik wetenschappelijk schrijver voor een laboratorium voor zoogdiergenetica. Destijds zouden de woorden \u201cin vivo base editing\u201d me met een vreugdekreet van mijn stoel hebben laten vallen! Ik deel Dr. Collins&#039; \u201cWOW,\u201d en ik ben zo dankbaar voor de helderheid en het optimisme van dit artikel.\u201d<\/em><\/p>\n<p><em>\u201cDank aan de auteur voor het verslaan van deze zeer belangrijke wetenschappelijke ontwikkeling. Een groot compliment aan Dr. Collins en iedereen bij PRF voor hun onvermoeibare werk. Ik was gelukkig en nederig om erbij te zijn toen PRF begon en ik heb met plezier vrijwilligerswerk gedaan voor veel van hun fondsenwervende initiatieven om hun ongelooflijke inspanningen te ondersteunen. Ik had het geluk om Sam meerdere keren te ontmoeten \u2013 hij was zo&#039;n geweldig persoon. Het is een waar genoegen om het succes te zien dat al dit harde werk heeft bereikt en blijft bereiken.\u201d<\/em><\/p>\n<p><em>\u201cDr. Collins is het soort wetenschapper dat we nodig hebben. Hij is niet op zoek naar miljoenen aan een medicijnbehandeling, maar hij leeft graag van zijn NIH-salaris terwijl hij het cruciale onderzoek doet dat levens redt. Meer zoals hij, graag!\u201d<\/em><\/p>\n<p><em>\u201cDit is geweldig en hoopvol. Ik had het geluk om Sam en zijn ouders te kennen. Ik denk nog steeds aan hem - zijn moed, vasthoudendheid en geweldige geest. Hij moedigt je zeker aan vanaf waar zijn reis hem heeft gebracht!\u201d<\/em><\/p>\n<p>[\/et_pb_testimonial][\/et_pb_column][\/et_pb_row][\/et_pb_section]<\/p>","protected":false},"excerpt":{"rendered":"<p>Het onderzoek is in volle gang: Zoals gemeld in de New York Times, zou de remedie voor Progeria in zicht kunnen zijn!! Onze samenwerkingen met topmensen in genbewerking werpen hun vruchten af en zijn, in de woorden van voormalig NIH-directeur Dr. Francis Collins, mogelijk \u201chet antwoord op een droom die we allemaal willen laten uitkomen.\u201d<\/p>","protected":false},"author":2,"featured_media":19157,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"on","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":"","_links_to":"","_links_to_target":""},"categories":[2,1],"tags":[],"class_list":["post-18802","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-news","category-uncategorized"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v26.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>NYT Article I The Progeria Research Foundation<\/title>\n<meta name=\"description\" content=\"Remarkable Progeria gene editing progress featured in NY 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