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Sekilas Agenda

Note: Agenda Subject to Change
Wednesday, October 29, 2025
Time Session Pembicara
  3:00-8:30 PM   Registration Desk Open & Poster Set-Up
  5:00-5:10 PM   Pengantar & Salam dari PRF Medical Director Leslie Gordon, MD, PhD,
Executive Director Audrey Gordon, Esq.,
Board Chair Scott Berns, MD, MPH, FAAP
  5:10-5:15 PM   Sponsor Remarks Riccardo Zanolli
  5:15-6:15 PM   “Coming of Age” Conversations:  Young Adults with HGPS as Research Partners Moderator: Merlin Waldron
Riccardo Zanolli
Kaylee Halko
  6:15-6:30 PM   Musical Kickoff Francis Collins, Dokter Spesialis Bedah Mulut dan Maksimal
  6:30-7:30 PM   Dinner & Networking
  7:30-8:30 PM   Poster Petir Bulat
Thursday, October 30, 2025
  7:15 AM-8:30 PM Registration Desk Open
  7:30-9:00 AM Bridging the Bench Mentor Session   Breakfast
 Hasil Uji Coba Pengobatan Progeria Saat Ini       Moderator: Mark Keiran, MD
  9:00-9:20 AM Uji Coba Pengobatan Lonafarnib dengan Riwayat Alami Jangka Panjang   Leslie Gordon, Dokter Spesialis Bedah Mulut dan Maksimal
  9:20-9:40 AM Uji Coba Klinis Progerin Fase 2a untuk Pengobatan Progeria   Monica Kleinman, Dokter Spesialis
  9:40-10:00 AM Break
 10:00-10:20 AM Tools for Pivotal Science and Medicine in Progeria: Biomarker Assay Development, Qualification and Reagent Generation   Barbara Natke, Doktor
 10:20-10:40 AM Evaluation of Coronary Artery and Aortic Calcium by Computed Tomography in Progeria   Dokter Sunil Ghelani
 10:40-12:00 PM Lunch
Cardiovascular Disease in HGPS and Aging       Moderator: Maria Eriksson, PhD
 12:00-12:20 PM Single-cell Analysis Reveals the Phenotypic Landscape of Arterial Cells in Progeria   Maria Eriksson, Doktor
 12:20-12:40 PM Title To Be Announced   Dokter Shannon Lyon
 12:40-1:00 PM Angiopoietin-2: A Potential Therapeutic Target for Vascular Protection in Hutchinson-Gilford Progeria Syndrome   Kan Cao, Doktor
  1:00-1:20 PM Break
  1:20-1:40 PM Progeria dan Kalsifikasi Vaskular: Diet dan Perawatan   Ricardo Villa Bellosta, Doktor
  1:40-2:00 PM Title To Be Announced   Ashwin Prakash, MD
  2:00-2:20 PM Title To Be Announced   Andrea Porzionato, PhD
  2:20-3:00 PM Break
  5:00-6:30 PM Dinner & Networking
  6:30-7:30 PM Poster Session Part 1   Even Numbered Posters
  7:30-8:30 PM Poster Session Part 2   Odd Numbered Posters
Friday, October 31, 2025
  8:00 AM-2:00 PM Registration Desk Open
  8:00-9:00 AM Breakfast & Networking

Progeria Treatment Discovery for a Healthy Future       Moderator: Francis Collins, MD, PhD

  9:00-9:20 AM Title To Be Announced   David Liu, Doktor
  9:20-9:40 AM ProSPER: PROgeria Streamlined Platform Gene Editing for Rare diseases   David Liu, PhD & Francis Collins, MD, PhD
  9:40-10:00 AM Development of Gene Silencing (RNAi) and Gene Editing Therapeutics for Hutchinson-Gilford Progeria Syndrome (HGPS)   Nizar Saad, Doktor
 10:00-10:20 AM Break  
 10:20-11:00 AM AI-driven Therapeutic Antisense Oligonucleotide for Hutchinson-Gilford Progeria   Ning Shen, Doktor
 11:00-11:20 AM First-Generation PROTACs for Improving Progeria Phenotype   Silvia Ortega Gutierrez, Doktor
 11:20-12:20 PM Lunch & Networking
Endocrine and GI Disease in Progeria       Moderator: Vicente Andres, PhD
 12:20-12:40 PM Lipodistrophy and Cardiovascular Pathology in Hutchinson-Gilford Progeria Syndrome   Vicente Andres, PhD
 12:40-1:00 PM Unraveling Accelerated Intestinal Ageing in HGPS Physiopathology: An Integrative Approach   Laurence Arbibe, Doktor
  1:00-1:20 PM Targeting Inflammation to Ameliorate HGPS Pathologies   Susana Gonzalo, Doktor
  1:20-1:40 PM Break  
  1:40-2:40 PM

Penutup Lokakarya
All-hands meeting discussion on key findings and highest priorities for future success.

  Leslie Gordon, Dokter Spesialis Bedah Mulut dan Maksimal
  Francis Collins, Dokter Spesialis Bedah Mulut dan Maksimal
  Mark Keiran, MD

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