So much progress, so much to share!! PRF’s 2024 newsletter is rife with exciting updates about our global work – supporting the most promising research toward better treatments and the CURE, and our strategic awareness efforts to find and help all children with Progeria around the world.
Inside, you’ll get:
- the full scoop on the brand-new clinical trial we’re supporting to determine whether the addition of a new drug to the current lonafarnib treatment is more effective than lonafarnib alone;
- a snapshot into the lives, hobbies and milestones of the children and young adults you support;
- updates on our other areas of discovery, in the cutting-edge areas of RNA therapeutics and gene therapy that we hope will be our ticket to the CURE.