PRF’s 12th International Scientific Workshop
October 29-31, 2025 A landmark meeting summary from the 12th International PRF Scientific Workshop has just been published in Nature…

For more than 25 years, PRF has been setting the standard for ultrarare disease research. Donor and volunteer support has made it possible to identify and support children and families worldwide, fund critical research, and develop therapies that would not exist otherwise. When no clear path from discovery to treatment existed, we built one.
And we’re not done.