
L'ordre du jour en un coup d'œilNote: Agenda Subject to Change |
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Wednesday, October 29, 2025 |
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Time | Session | Conférencier |
3:00-8:30 PM | Registration Desk Open & Poster Set-Up | |
5:00-5:10 PM | Présentation et salutations de la PRF | Medical Director Leslie Gordon, MD, PhD, Executive Director Audrey Gordon, Esq., Board Chair Scott Berns, MD, MPH, FAAP |
5:10-5:15 PM | Sponsor Remarks | Riccardo Zanolli |
5:15-6:15 PM | “Coming of Age” Conversations: Young Adults with HGPS as Research Partners | Moderator: Merlin Waldron Riccardo Zanolli Nathan Falcone Michiel Vandeweert |
6:15-6:30 PM | Musical Kickoff | Dr Francis Collins, Ph. D. |
6:30-7:30 PM | Dinner & Networking | |
7:30-8:30 PM | Affiche ronde éclair |
Thursday, October 30, 2025 |
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7:15 AM-8:30 PM | Registration Desk Open | ||
7:30-9:00 AM | Bridging the Bench Mentor Session | Breakfast | |
Résultats des essais thérapeutiques actuels sur la progéria Moderator: Mark Keiran, MD | |||
9:00-9:20 AM | Essai de traitement à long terme par lonafarnib sur l'histoire naturelle | Dr Leslie Gordon, Ph. D. | |
9:20-9:40 AM | Essai clinique de phase 2a sur la progérine dans le traitement de la progéria | Dr Monica Kleinman | |
9:40-10:00 AM | Break | ||
10:00-10:20 AM | Tools for Pivotal Science and Medicine in Progeria: Biomarker Assay Development, Qualification and Reagent Generation | Barbara Natke, Ph. D. | |
10:20-10:40 AM | Evaluation of Coronary Artery and Aortic Calcium by Computed Tomography in Progeria | Dr Sunil Ghelani | |
10:40-12:00 PM | Lunch | ||
Cardiovascular Disease in HGPS and Aging Moderator: Maria Eriksson, PhD | |||
12:00-12:20 PM | Single-cell Analysis Reveals the Phenotypic Landscape of Arterial Cells in Progeria | Maria Eriksson, Ph. D. | |
12:20-12:40 PM | Title To Be Announced | Dr Shannon Lyon | |
12:40-1:00 PM | Angiopoietin-2: A Potential Therapeutic Target for Vascular Protection in Hutchinson-Gilford Progeria Syndrome | Kan Cao, Ph. D. | |
1:00-1:20 PM | Break | ||
1:20-1:40 PM | Progeria et calcification vasculaire : régime alimentaire et traitements | Ricardo Villa Bellosta, Ph. D. | |
1:40-2:00 PM | Title To Be Announced | Ashwin Prakash, MD | |
2:00-2:20 PM | Title To Be Announced | ||
2:20-3:00 PM | Break | ||
5:00-6:30 PM | Dinner & Networking | ||
6:30-7:30 PM | Poster Session Part 1 | Even Numbered Posters | |
7:30-8:30 PM | Poster Session Part 2 | Odd Numbered Posters |
Friday, October 31, 2025 |
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8:00 AM-2:00 PM | Registration Desk Open | ||
8:00-9:00 AM | Breakfast & Networking | ||
Progeria Treatment Discovery for a Healthy Future Moderator: Francis Collins, MD, PhD |
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9:00-9:20 AM | Title To Be Announced | David Liu, Ph. D. | |
9:20-9:40 AM | ProSPER: PROgeria Streamlined Platform Gene Editing for Rare diseases | David Liu, PhD & Francis Collins, MD, PhD | |
9:40-10:00 AM | Development of Gene Silencing (RNAi) and Gene Editing Therapeutics for Hutchinson-Gilford Progeria Syndrome (HGPS) | Nizar Saad, Ph. D. | |
10:00-10:20 AM | Break | ||
10:20-11:00 AM | AI-driven Therapeutic Antisense Oligonucleotide for Hutchinson-Gilford Progeria | Ning Shen, Ph. D. | |
11:00-11:20 AM | First-Generation PROTACs for Improving Progeria Phenotype | Silvia Ortega Gutierrez, Ph. D. | |
11:20-12:20 PM | Lunch & Networking | ||
Endocrine and GI Disease in Progeria Moderator: Vicente Andres, PhD | |||
12:20-12:40 PM | Lipodistrophy and Cardiovascular Pathology in Hutchinson-Gilford Progeria Syndrome | Vicente Andres, PhD | |
12:40-1:00 PM | Unraveling Accelerated Intestinal Ageing in HGPS Physiopathology: An Integrative Approach | Laurence Arbibe, Ph. D. | |
1:00-1:20 PM | Targeting Inflammation to Ameliorate HGPS Pathologies | Susana Gonzalo, Ph. D. | |
1:20-1:40 PM | Break | ||
1:40-2:40 PM |
Bilan de l'atelier |
Dr Leslie Gordon, Ph. D. |