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Speakers to date, subject to change as speakers are added and confirmed.

Sammy, Amerigo and Laura Basso, Italy

Sammy, Amerigo and Laura Basso, Italy

Family Panel

The Journey from No Hope, to Clinical Trials, and Entering Young Adulthood – Living Life to Its Fullest
Vicenza, Italy

David R. Liu, PhD

David R. Liu, PhD

Keynote Speaker

The Power and Potential of Genetic Editing in Science and Medicine
Howard Hughes Medical Institute, Broad Institute, Harvard University

Leslie Gordon, MD, PhD

Leslie Gordon, MD, PhD

Medical Director and Chair, Organizing Committee

FDA Biomarker Program – Progerin as a Biomarker for HGPS
and Moderator: Progerin Biology and HGPS Model Systems

The Progeria Research Foundation, Brown University, Hasbro Children’s Hospital, Boston Children’s Hospital, and Harvard
University

Vicente Andrés, PhD

Vicente Andrés, PhD

Scientific Organizing Committee

Generation of Transgenic Lamin C-Stop (LCS) and CAG-Cre Yucatan
Minipigs to Breed HGPS Yucatan Minipigs for Preclinical Trials
and Moderator: Cardiovascular Disease in HGPS and Aging
CNIC, Spanish National Cardiovascular Research Center, Madrid, Spain

Judy Campisi, PhD

Judy Campisi, PhD

Scientific Organizing Committee

Moderator: Molecular and Cellular Mechanisms in HGPS and Aging
and Summation of Key Findings Panel

Buck Institute on Aging, Palo Alto, CA
Mark Kieran, MD, PhD

Mark Kieran, MD, PhD

Scientific Organizing Committee

Moderator: Treatments and Trials on the Horizon
Bristol-Meyers Squibb
Francis Collins, MD, PhD

Francis Collins, MD, PhD

RNA and DNA Therapeutics for Progeria
Director, National Institutes of Health, Bethesda, MD

Martin Bergö, PhD

Martin Bergö, PhD

Preclinical Develoopment of ICMT Inhibitors for HGPS Therapy
Karolinska Institutet, Stokholm, Sweden

Abigail Buchwalter, PhD

Abigail Buchwalter, PhD

Defining the Feasibility of Progerin Clearance as a Therapy for HGPS
University of California, San Francisco

David Cory

David Cory

Rare Disease Pharma and The Journey Towards Lonafarnib Approval
Eiger BioPharmaceuticals, Inc., Palo Alto, CA
Roland Foisner, PhD

Roland Foisner, PhD

Endothelial Progerin Initiates a Sensesce-Linked Profibrotic and Pro-Inflammatory Signaling
Max F. Perutz Lab’s, Medical University, Vienna, Austria

Marie Gerhard-Herman, MD

Marie Gerhard-Herman, MD

Clinical Cardio-Neurovascular Panel: Patient-Centered Research Progress on Clinical Cardio-Neurovascular Disease in Progeria and Aging
Brigham &Women’s Hospital, Boston
Monica Kleinman, MD

Monica Kleinman, MD

Phase I/II Trial of Everolimus with Lonafarnib for Progeria
Boston Children’s Hospital
Giovanna Lattanzi, PhD

Giovanna Lattanzi, PhD

Improving the Quality of Life in Progeria: an IL-6 Receptor Antibody
Murine Treatment Trial with Tocilizumab
CNR Institute of Molecular Genetics, Bologna, Italy
Tom Misteli, PhD

Tom Misteli, PhD

Mechanisms and Therapeutic Applications in HGPS
and Summation of Key Findings Panel
National Cancer Institute, National Institutes of Health, Bethesda, MD
Srinivasan Mukundan, MD, PhD

Srinivasan Mukundan, MD, PhD

Clinical Cardio-Neurovascular Panel: Patient-Centered Research Progress on Clinical Cardio-Neurovascular Disease in Progeria and Aging
Brigham &Women’s Hospital, Boston
Francesco Musumeci, MD

Francesco Musumeci, MD

Clinical Cardio-Neurovascular Panel: Patient-Centered Research Progress on Clinical Cardio-Neurovascular Disease in Progeria and Aging
Azienda Ospedaliera San Camillo Forlanini, Italy
Bum-Joon Park, PhD

Bum-Joon Park, PhD

Effect of Progerinin (SLC-D011) and Lonafarnib on HGPS: A Combined in Vitro and in Vivo Study
Pusan National University, South Korea
Ashwin Prakash, MD

Ashwin Prakash, MD

Clinical Cardio-Neurovascular Panel: Patient-Centered Research Progress on Clinical Cardio-Neurovascular Disease in Progeria and Aging
Boston Children’s Hospital, Boston, MA

Catherine Shanahan, PhD

Catherine Shanahan, PhD

What Progeria has Taught us About Vascular Smooth Muscle Cell Ageing
Kings College London, England
Leslie Smoot, MD

Leslie Smoot, MD

Clinical Cardio-Neurovascular Panel: Patient-Centered Research Progress on Clinical Cardio-Neurovascular Disease in Progeria and Aging
Boston Children’s Hospital, Boston, MA

Colin Stewart, PhD

Colin Stewart, PhD

Breaking the LINC to Treat Progeria
Institute of Medical Biology, Immunos, Singapore