SCIENTIFIC COMMITTEE
LESLIE Gordon, MD, PhD
The Progeria Research Foundation, Medical Director
Scientific Committee Chair
Speaker and Moderator
Introduction & Greetings; Long-term Natural History Lonafarnib Treatment Trial; Workshop Wrap-Up
Vincente Andres, PhD
Centro Nacional de Investigaciones Cardiovasculares Carlos III
Speaker and Moderator
Lipodystrophy in Progeria and Aging
Maria Eriksson, PhD
Karolinska Institute
Speaker
Single-cell analysis reveals the phenotypic landscape of arterial cells in Progeria
Mark Kieran, MD, PhD
Day One Biopharmaceuticals, VP Clinical Development
Moderator
Current Treatment Trial Outcomes in Progeria
Workshop Wrap-Up
SPEAKERS
Laurence Arbibe, MD, PhD
INSERM Institut Necker Enfants Malades
Speaker
Unraveling accelerated intestinal ageing in HGPS physiopathology: an integrative approach
Scott Berns, MD, MPH, FAAP
The Progeria Research Foundation, Board Chair
Speaker
Introduction & Greetings
Kan Cao, PhD
University of Maryland College Park
Speaker
Angiopoietin-2 reverses endothelial cell dysfunction in progeria vasculature
Francis Collins, MD, PhD
Center for Precision Health Research National Human Genome Research Institute National Institutes of Health, NIH Distinguished Lecturer
Speaker and Moderator
Musical Introduction; ProSPER: PROgeria Streamlined Platform gene Editing for Rare diseases; Workshop Wrap-Up
Nathan Falcone
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
Sunil Ghelani, MD
Boston Children’s Hospital, Attending Cardiologist
Speaker
First-ever Aortic and Coronary Artery Calcium Computed Tomography Clinical Trial Study in Progeria
Susana Gonzalo, PhD
Dpt. Biochemistry and Molecular Biology St Louis University School of Medicine, Professor
Speaker
Cathepsin-L mediated remodeling of the nuclear proteome
Audrey Gordon, Esq.
The Progeria Research Foundation, Executive Director
Speaker
Introduction & Greetings
Sheila Hegde, MD
Brigham and Women’s Hospital
Speaker
New discoveries in Cardiac Measures of Disease in Progeria and Aging through Echocardiography
Monica Kleinman, MD
Boston Children’s Hospital and Harvard Medical School
Speaker and Moderator
Phase 2a Progerin in Clinical Treatment Trial for Progeria
David Liu, PhD
Broad Institute
Speaker
ProSPER: PROgeria Streamlined Platform gene Editing for Rare diseases
Shannon Lyon, MD
Brigham and Women’s Hospital
Speaker
New discoveries in Cardiac Measures of Disease in Progeria and Aging through Echocardiography
Barbara Natke, PhD
The Progeria Research Foundation, Chief Operating Officer and Biomarker Lead
Speaker
Tools for Pivotal Science and Medicine in Progeria: Antibody and Biomarker Assay Development
Megan Nighbor
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
Silvia Ortega Gutierrez, PhD
Universidad Complutense de Madrid
Speaker
Reduction of progerin levels by small molecules as a new approach for treating Progeria
Griffin Ray
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
Nizar Saad, PhD
Abigail Wexner Research Institute, Nationwide Children’s Hospital
Speaker
Development of a miRNA-based Gene Therapy for Hutchinson-Gilford Progeria Syndrome (HGPS)
Keri Shafer, MD
UT Southwestern Medical Center
Speaker
New discoveries in Cardiac Measures of Disease in Progeria and Aging through Echocardiography
Ning Shen, PhD
Liangzhu Laboratory, Zhejiang University School of Medicine, Professor
Speaker
AI-driven therapeutic antisense oligonucleotide for Hutchinson-Gilford Progeria
Michiel Vandeweert
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
Ricardo Villa Bellosta, PhD
Center for Research in Molecular Medicine and Chronic Diseases, Group Leader, Ramon y Cajal Researcher
Speaker
Progeria and Vascular Calcification: Diet and Treatments
Merlin Waldron
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
Ricardo Zanolli
Panelist
“Coming of Age” Conversations: Young adults with HGPS as Research Partners
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